Thanks for the summary which seems to confirm my fears that this documentary will argue that 'high' cost therapies for "a few rare diseases" are not worth paying for.
Judging by the example cost quoted -up to "a quarter of a million pounds per patient" - I would point out that this kind of figure reflects costs for drugs developed for rare inherited diseases - ie. orphan drugs to treat children- very very rare and thus not using a high proportion of the overall NHS budget.
Appraisals of such orphan treatments are currently dealt with by AGNSS - an Advisory Group For National Specialised Services- soon to be taken over by NICE- in April this year.
AGNSS was set up to advise the Secretary of State for Health on which specialised services and technologies should or should not be commissioned nationally.
'... a 2011 review of NICE appraisals by the Office of Health Economics (OHE) shows that only five orphan drugs of the 74 approved by the EMA were assessed by the middle of the year, with three of these not recommended for use.
The Scottish Medicines Consortium (SMC) in sharp contrast assessed 55 of these drugs.
NICE’s minimal assessment is likely due to fact that its methodology may result in a negative recommendation for an orphan drug, thus leading to a severe public backlash.'
See.....
http://healthcare.blogs.ihs.com/2012/02/06/agnss-is-there-really-a-need-...
I can only guess at why BBC Scotland have commissioned a documentary like this at this time!
I have asked for reassurance from the makers that they are not sending the message that we- as a society- cannot afford to treat patients with rare diseases due to the cost of any particular drug - and the money could/should be diverted elsewhere?
Presumably- if this is their argument- they would advise that parents and families of children born with very rare inherited conditions should do what- pay privately/accept that their child's life is going to be short?
I understand that they have included CML as an example-maybe because the therapy is so successful- and therefore the population of CML patients is increasing year on year and represents a high cost to NHS?
I assume this is why they flew over to Portland OR, to interview Brian Druker! (tax payers paying for the fight/hotel costs?)
Sandy